Treatment for Cystic Fibrosis: Vertex Acquires Concert’s CFTR Potentiator CTP-656
Vertex Pharmaceuticals recently purchased the Phase 2 cystic fibrosis potentiator drug CTP-656 from Concert Pharmaceuticals. The deal is estimated to […]
Mom takes on Vertex CEO about pricey Cystic Fibrosis Treatment Drugs
In October, Oklahoma-based journalist and mom Juliana Keeping traveled to Boston with her son to confront Jeffrey Leiden, the CEO of […]
Individual Counseling Offered
jricci brings us this great news: Through a very generous contribution Financial Support for Individual Counseling Services are being offered […]
We Lobby
A Brief History of Our Lobbying Efforts in 2015 In April, 2015, we sent this letter to the FDA […]
Trial results of Ivacaftor in Cystic Fibrosis children ages 2-5
Results are out from a two part study involving children ages 2-5 with at least one gating mutation trying Ivacaftor […]